AskBio’s gene therapy shows promising 12-month results for heart failure
Results demonstrate favorable safety profile and clinically meaningful improvements in patients with non-ischemic heart failure
Results demonstrate favorable safety profile and clinically meaningful improvements in patients with non-ischemic heart failure
Adverum's lead program, Ixo-vec, is a Phase 3 gene therapy designed to treat vision loss associated with wet age-related macular degeneration with a single intravitreal dose
Several technologies for hemoglobinopathies are being transferred to commercial partners
New offering to debut at the 32nd ESGCT Congress, October 7–10, 2025, in Seville, Spain
Lonza boosts TheraPEAK line with new Cytokines and AAV Medium for next-gen therapies
NouvNeu001 is the world’s first allogeneic iPSC-derived cell therapy for Parkinson’s disease to receive this designation
Collaboration reinforces Boehringer Ingelheim’s expertise in microbial contract development and manufacturing
Rocket will also collaborate with investigators to implement an immunomodulatory regimen more closely reflecting that administered in the Phase 1 pediatric cohort
Elevidys is currently the only approved gene therapy that targets the root cause of Duchenne
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