Clinical Trials | December 22, 2025
Ipsen’s FALKON trial falls short in rare FOP study, offers key insights
FOP is a rare genetic disorder caused by mutations in the ALK2 kinase
FOP is a rare genetic disorder caused by mutations in the ALK2 kinase
Alport Syndrome is caused by genetic mutations affecting type IV collagen in the kidneys, ears, and eyes
Approval based on pivotal KOMET Phase III trial demonstrating significant tumour reduction in adults with NF1
BIL also holds an option to increase its equity stake by an additional 15%
CSIR-IGIB advances indigenous CRISPR Trials on sickle cell anaemia, anti-microbial resistance, liver fibrosis and rare disorders
Dr. Prabhavathi brings over 14 years of unparalleled experience in pediatrics and a specialized focus on neurodevelopmental disorders
Modi remarked that more than 20 illustrious research institutions such as IISc, IITs, CSIR and DBT-BRIC have played a major role in this research
Aromatic L-amino acid decarboxylase deficiency is a rare genetic disorder that affects the production of some neurotransmitters
NULIBRY is a first-in-class synthetic cPMP substrate replacement therapy to reduce the risk of mortality in patients with MoCD Type A
The partners will collaborate to build a cutting-edge oligonucleotide cGMP manufacturing facility
Subscribe To Our Newsletter & Stay Updated
