Latest news and insights on the pharmaceutical industry | Indian Pharma Post | Page 20

Results For "rare-disease"

212 News Found

Aadi Bioscience secures U.S FDA approval of its first product Fyarro
Drug Approval | November 26, 2021

Aadi Bioscience secures U.S FDA approval of its first product Fyarro

Fyarro is the first and only approved therapy for adults for the treatment of malignant PEComa in adults


Novo Nordisk to acquire Dicerna Pharmaceuticals for US $ 3.3 bn
Biotech | November 20, 2021

Novo Nordisk to acquire Dicerna Pharmaceuticals for US $ 3.3 bn

Dicerna develops RNAi-based therapies to selectively silence genes that cause or contribute to disease


U.S. FDA approves first drug to improve growth in kids with most common form of dwarfism
Drug Approval | November 20, 2021

U.S. FDA approves first drug to improve growth in kids with most common form of dwarfism

Achondroplasia is a genetic condition that causes severely short stature and disproportionate growth


World’s first Whole Genome Sequencing study uncovers new and potential therapies
News | November 12, 2021

World’s first Whole Genome Sequencing study uncovers new and potential therapies

The ground-breaking project, led by Genomics England and NHS England, was established in 2013 to sequence 100,000 whole genomes from NHS patients and their families


LifeCell Diagnostics expands newborn screening portfolio
Clinical Trials | November 11, 2021

LifeCell Diagnostics expands newborn screening portfolio

LSDCheck is CE-IVD approved LCMSMS-based testing kit for LSD in newborns


Takeda receives the Arogaya CIBioD Leadership Award
Public Health | November 10, 2021

Takeda receives the Arogaya CIBioD Leadership Award

It was recognized for its holistic initiatives designed to improve the quality of life and standards of care for patients


SOPHiA Genetics launches SOPHiA DDM to assist Agilent customers
Digitisation | November 02, 2021

SOPHiA Genetics launches SOPHiA DDM to assist Agilent customers

New bioinformatic workflow advances analysis capabilities for whole-exome assessment and interpretation


Rainbow hospital gives new lease of life to infant on ECMO support
Healthcare | October 28, 2021

Rainbow hospital gives new lease of life to infant on ECMO support

The youngest child in India to survive ECMO after undergoing bone marrow transplant for a rare disease


Thermo Fisher Scientific unveils Q Digital PCR system
Medical Device | October 28, 2021

Thermo Fisher Scientific unveils Q Digital PCR system

It is the first integrated digital PCR solution ideal for oncology, cell and gene therapy development


WuXi ATU opens manufacturing facility in Shanghai to enhance its CTDMO services
Biotech | October 22, 2021

WuXi ATU opens manufacturing facility in Shanghai to enhance its CTDMO services

It’s the company’s fourth manufacturing site worldwide. Others are located in the US, UK and China