ASMD is highly variable and the age of onset, specific symptoms and severity of the disorder can vary dramatically from one person to another
These initiatives aim to improve access to healthcare for rare disease patients
Receives Subject Expert Committee recommendation to bring new therapies of Pompe, ASMD to India
Dr Ratna Puri from Sir Ganga Ram Hospital, Delhi is the Chairperson of the expert committee.
Early stage projects of up to Rs. 9 crore eligible for up to Rs. 5 crore assistance and later stage projects of up to Rs. 285 crore eligible for up to Rs. 100 crore assistance
The Moderna Innovation and Technology Centre in Harwell, Oxfordshire is now fully operational and Moderna is licensed to supply British-made COVID-19 vaccines to the UK population
Collaboration matches more eligible patients, including those with rare and complex diseases, to appropriate clinical trials
ITP is a disease of complex immune dysregulation leading to low platelet counts, bleeding, and reduced quality of life
Sarepta has also entered into an agreement with Arrowhead to transfer 2,660,989 shares of Arrowhead common stock in satisfaction of $50 million of the company’s previously announced $100 million milestone payment obligation
Subscribe To Our Newsletter & Stay Updated
