FDA grants ODD to Keros KER-065 for treatment of Duchenne muscular dystrophy
KER-065 is a novel ligand trap comprised of a modified ligand-binding domain derived from activin receptor type IIA and activin receptor type IIB
KER-065 is a novel ligand trap comprised of a modified ligand-binding domain derived from activin receptor type IIA and activin receptor type IIB
Elevidys is currently the only approved gene therapy that targets the root cause of Duchenne
Capricor’s BLA for Deramiocel received Priority Review in March 2025
The primary endpoint in the final analysis was assessed by change in the North Star Ambulatory Assessment at one year after treatment
FDA requests Sarepta Therapeutics to suspend distribution of Elevidys and places clinical trials on hold for multiple gene therapy products following 3 deaths
Deflazacort is a corticosteroid indicated for the treatment of Duchenne muscular dystrophy (DMD) in patients 5 years of age and older
Biopharma can benefit from the critical enablers of innovation in the private healthcare system in India
Study efficacy measures will include the expression of dystrophin protein and motor function.
Additional data across neurological disorders, including Alzheimer’s disease, help advance the scientific understanding of these conditions and the potential impact of early treatment
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