Investigational therapy efzimfotase alfa shows promising Phase III results in rare bone disease
Efzimfotase alfa is an investigational enzyme replacement therapy designed to reduce injection volume
Efzimfotase alfa is an investigational enzyme replacement therapy designed to reduce injection volume
High-level results from the Phase III OBERON and TITANIA trials revealed that the first-in-class monoclonal antibody reduced the annual rate of moderate-to-severe COPD exacerbations compared with placebo
The collaboration highlights the rising importance of intranasal delivery in developing non-vaccine approaches to respiratory disease prevention
There are limited treatment options available for patients living with non-diabetic CKD, and the unmet need is high for new treatments to delay kidney disease progression and reduce cardiovascular risk
Giredestrant shows promise despite missing primary goal
Gazyva/Gazyvaro outperformed placebo across all key and secondary endpoints
Iza-bren met both dual primary endpoints, delivering statistically significant and clinically meaningful improvements in progression-free survival
The results mark a potential breakthrough for patients living with CIndU, a condition with limited treatment options
A final tranche of €12 million will follow, contingent on positive pivotal study results, with the share price calculated according to an agreed formula
The Phase III programme, Enith1 and Enith2, is expected to launch this quarter
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