The FDA setback highlights ongoing tensions between patient needs, regulatory processes, and the use of real-world evidence in evaluating treatments for rare diseases
Currently, Sharma is a part of the Philippines Country Leadership Team as Business Unit Head Respiratory & Immunology
ASMD is highly variable and the age of onset, specific symptoms and severity of the disorder can vary dramatically from one person to another
These initiatives aim to improve access to healthcare for rare disease patients
Receives regulatory approval for its molecule ‘Selumetinib’ in India
Receives Subject Expert Committee recommendation to bring new therapies of Pompe, ASMD to India
TMA will leverage Syntegra's synthetic data engine to accelerate the building of predictive diagnostic algorithms
Takeda and United Nations Global Compact Network of India (UNGCNI) join hands
Three RFPs now open for qualified researchers through NORD's Jayne Holtzer rare disease research grants program
Dr Ratna Puri from Sir Ganga Ram Hospital, Delhi is the Chairperson of the expert committee.
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