Syntegra partners with TMA Precision to reduce the diagnostic odyssey for rare disease with synthetic data-enabled tools

TMA will leverage Syntegra's synthetic data engine to accelerate the building of predictive diagnostic algorithms

Strengthening the access to rare disease treatment in India

Takeda and United Nations Global Compact Network of India (UNGCNI) join hands

NORD announces over US $ 100,000 in grant funding available for rare disease research

Three RFPs now open for qualified researchers through NORD's Jayne Holtzer rare disease research grants program

Dr Sheela Nampoothiri appointed as co-chair of ICMR's Rare Diseases expert committee

Dr Ratna Puri from Sir Ganga Ram Hospital, Delhi is the Chairperson of the expert committee.

Cytel and Pulse Infoframe to transform rare disease research landscape

Both companies will combine their expertise to channel real-world evidence toward ground-breaking new treatments in rare diseases

FDA nod to first treatment for rare genetic brain disorder

The approval comes after a systematic review of published literature

UK pushes space-made medicines from orbit to patients with new support package

The initiative provides clearer regulatory guidance and a defined path from research in space to patient access on Earth

Lonza expands manufacturing pact with Genetix to meet rising demand for gene therapy ZYNTEGLO

Merck delivers resilient 2025 performance despite global headwinds

Strong performances in its Life Science, Healthcare and Electronics divisions — particularly Process Solutions, Cardiovascular treatments and Semiconductor Materials — powered the company’s results

FDA okays JUXTAPID for kids with ultra-rare genetic cholesterol disorder